PTC Therapeutics

PTC's President & CEO Matthew Klein, MD and CFO Pierre Gravier will speak at two upcoming investor conferences to close out the year. Learn more: ow.ly/O5yv5102X14

Today we announced our Q3 2026 financial results where we highlighted our continued commercial momentum and raised full-year revenue guidance. Read the press release: ow.ly/CVBZ5102ghh | Webcast: ow.ly/23Qw5102ghi

PTC will host a web conference to report our third quarter 2026 financial results and provide an update on the company’s business on Thursday, Oct. 29, 2026, at 4:30 p.m. ET. Learn more: ow.ly/hHoP50ZY969

Hello, #FabryDisease community. We're honored to introduce ourselves as we advance the investigational gene therapy ST-920 with an FDA submission planned before the end of 2026. Read our letter to the community: ow.ly/XhNx50ZTegw

PTC will participate in three upcoming investor conferences in September. Learn more: ow.ly/5sSy50ZG4kj

#SSIEM2026 is a meaningful moment for the PKU community. At the meeting multiple scientific data presentations spanning research, clinical outcomes & real-world case studies will be featured. ow.ly/cbU150ZEJTG

PTC Therapeutics was selected as the winning bidder to acquire ST-920 – a BLA-stage one-time administered AAV gene therapy for Fabry disease – from Sangamo Therapeutics in a competitive bankruptcy auction. Learn more: ow.ly/O0ie50Zz6cz

PTC Therapeutics welcomes Hege Sollie-Zetlmayer to its Board of Directors. With 30 years experience in biopharma and medical devices, including eight at PTC as CHRO, she brings deep global leadership to advance our mission for patients with rare diseases.

Today we announced our Q2 2026 financial results, highlighting strong commercial momentum with accelerating global uptake of our treatment for PKU. Learn more in our press release: ow.ly/Z4Tv50ZuPSH | Webcast: ow.ly/9GWI50ZuPST

PTC will host a web conference to report our second quarter 2026 financial results and provide an update on the company’s business on Thursday, July 30, 2026, at 4:30 p.m. ET. Learn more: ow.ly/Cr3a50Zojcl

Every day, the #PKU community faces unseen challenges. This #InternationalPKUDay, PTC is making a #PledgeForPKU: to listen, learn and support everyone this journey. Join us in championing hope, access and a future without limits. ow.ly/QosX50ZhKTo

Ahead of International PKU Day, we’re spotlighting mental health in the PKU community. Kevin, Signe & Regina share their journeys with stigma, anxiety & resilience. Learn more about their stories: ow.ly/YqMQ50ZbgLL

Our 2025 Corporate Social Responsibility Report highlights a year of focus, execution and measurable progress delivering differentiated medicines for people with rare disorders. See how we're driving impact across access, innovation, people & our planet: ow.ly/gwTR50Z6RRt

On #ClinicalTrialsDay, we honor patients, families, and clinical teams advancing rare disease research. This year's #ResearchRising theme reminds us that progress comes from partnership and trust. Learn more: ow.ly/wJiY50Z1Ml5

May is Friedreich’s ataxia (FA) Awareness Month and we're proud to honor the strength of those living with this rare condition. Kailey’s journey reflects the challenges many face, from recognizing symptoms to finding support. Learn more: ow.ly/KkRx50YZAmQ

Some days, the hardest part of living with a rare disorder isn’t what others can see—it’s the uncertainty: navigating genetic testing barriers and painful life changes. During #HDAwarenessMonth, PTC is proud to share stories like April's. Learn more: ow.ly/F1os50YWhRo

Today, we announced our Q1 2026 financial results, highlighting record performance and continued momentum across the business—led by the global launch of our treatment for #PKU. See the release: ow.ly/lbyh50YWi0T and webcast recording: ow.ly/5l7u50YWi1B

PTC will participate in three upcoming investor conferences in May and June. Learn more: ow.ly/sGsN50YVbXo

This #NationalPKUAwarenessMonth, we’re honoring the resilience of the PKU community. Living with PKU is more than a diet—it takes constant planning, advocacy and support. Amanda’s story, alongside her mom Jill, helps make the invisible visible. Learn more: ow.ly/kfKX50YTBSG

On Rare Disease Day, we recognize the millions living with rare conditions. At PTC, we know that progress starts with listening to those impacted. Together, we can make a difference. Learn more: ow.ly/pwXK50YliIh