MDA is the #1 voluntary health organization in the United States for people living with #MuscularDystrophy, #ALS, and related #neuromuscular diseases.
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Joined June 2009
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Muscular Dystrophy Association retweeted
Tim Green reflects on nearly a decade with ALS ahead of Wings Over Wall Street Gala 7ny.tv/zjsNei
ALT Tim Green reflects on nearly a decade with ALS ahead of Wings Over Wall Street Gala
Muscular Dystrophy Association retweeted
Pierre Deny, a French actor best known for his role in Netflix’s “Emily in Paris,” died on Monday from ALS-related complications. He was 69.
Deny played Louis de Léon — the CEO of luxury fashion company JVMA and father of Nicolas (Paul Forman), the love interest of Mindy (Ashley Park) — in Season 3 and 4 of the hit series.
variety.com/2026/tv/global/p…
Muscular Dystrophy Association retweeted
We've resubmitted our BLA to the FDA for our investigational, muscle-targeted treatment for SMA! Our progress reaffirms the promise of myostatin biology as we continue to prioritize scientific advancement & the needs of children & adults living with SMA. bit.ly/4sIxX9x
Muscular Dystrophy Association retweeted
🚨 NIH funding vote THIS WEEK. Rare disease research is on the line. 🦓
We dropped a breaking news episode of DNA Today (Ep. 378) on what’s at stake.
👉 Senate vote this week so urger your senators to support the NIH with @MDAorg's tool: MDA.org/SupportNIH
Muscular Dystrophy Association retweeted
Yesterday, Solid Biosciences shared an important update with the Friedreich’s ataxia community. The first participant has been dosed in the Phase 1b FALCON trial evaluating SGT-212, our novel, investigational dual-route administration gene therapy for the treatment of FA.
We are deeply grateful to the FA community, @CureFA_org, our clinical partners, and the patients and families whose trust and participation make this work possible. Your partnership continues to guide our mission to advance meaningful therapies for people living with FA. Read the full community letter here: solidbio.com/letter-to-the-f…
#FriedreichsAtaxia #FACommunity #RareDiseaseResearch
Muscular Dystrophy Association retweeted
The Muscular Dystrophy Association has opened applications for its 2026 college scholarship program for students with neuromuscular disease. musculardystrophynews.com/ne…
#musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD
ALT A person in a baseball cap speaks into a megaphone.
Muscular Dystrophy Association retweeted
You may know me from Grey’s Anatomy as Joe the bartender — or from appearances on Modern Family, You, Chicago Fire, or some other appearance.
I would like to share something important with you about my life and my career.
🧵👇
Muscular Dystrophy Association retweeted
Amyotrophic lateral sclerosis is a progressive neurodegenerative disease. Here's what you need to know about ALS, from risk factors to new treatments, medications, and clinical trials. health.usnews.com/conditions…
Muscular Dystrophy Association retweeted
We announced positive topline results from our Phase 1/2 DELIVER trial of z-rostudirsen in DMD: REC met its primary endpoint & maintained a favorable safety profile. Read more: bit.ly/3Yku2Sx
Muscular Dystrophy Association retweeted
Today we announced the completion of enrollment in the AFFINITY DUCHENNE® pivotal trial of RGX-202, our differentiated investigational gene therapy for Duchenne, as well as progress towards our planned commercial launch. Learn more: ir.regenxbio.com/news-releas… $RGNX
Muscular Dystrophy Association retweeted
Excited to welcome Dr. Sharon Hesterlee from @MDAorg as a session chair at TREAT-NMD Conference 2026!
She’ll lead a key session on Patient Involvement in Clinical Trials this Feb in Lisbon 🇵🇹
🔗 Register now: treat-nmd.org/conference/
#RareDisease #ClinicalTrials #Neuromuscular
Muscular Dystrophy Association retweeted
Through a joint effort of clinicians, researchers, and advocacy leaders, the @MDAorg and @ParentProjectMD announced the publication of new guidelines that promote the delivery and monitoring of gene therapy 🧬 in patients with DMD.
Read more: hubs.li/Q03Jpm4_0
Muscular Dystrophy Association retweeted
September 11 is a reminder of what fire fighters give in service to others.
We honor those who died so others could live, and those we continue to lose to 9/11-related illness, by carrying their memory forward – today and every day.
Muscular Dystrophy Association retweeted
Asked what strong means. I said “mental and emotional.” Dad heard “push-ups.” 🙄 Donate $35.75+ to @MDAorg, snag the tee, and support people living with ALS and other neuromuscular diseases. Use my link to donate bit.ly/BrookeMDADonate
Link in bio.
#Ad #MDAstrong #MDA75 #MDA
Muscular Dystrophy Association retweeted
We announced data from our positive Phase 3 trial in generalized #MyastheniaGravis (#gMG). Our research efforts underscore the potential of our pioneering approach using siRNA, which may offer a new type of treatment option for those suffering with this disease.
Muscular Dystrophy Association retweeted
Today we announced that the @US_FDA has granted Breakthrough Therapy Designation to DYNE-251 for the treatment of patients with DMD amenable to exon 51 skipping. Read here: bit.ly/4fly055
Muscular Dystrophy Association retweeted
From 25+ FDA-approved therapies to expert care for 70,000+ people each year, IAFF members are creating real change with @MDAorg.
Read more about the @IAFFofficial's Fill the Boot impact in the latest issue of our Fire Fighter International magazine:
Muscular Dystrophy Association retweeted
We were honored to attend the @MDAorg's 25th Annual Wings Over Wall Street Gala in NYC! We joined researchers, advocates & families, all united by one cause – a world free from ALS. 25 years strong and still going. #WOWS25 #ALSAdvocacy
Muscular Dystrophy Association retweeted
Today, the U.S. Senate passed a bill making devastating cuts to Medicaid & other health programs that the #neuromuscular community relies on to build healthy lives & independence.
Urge the House to reject this bill & its cuts NOW!
Read #MDA's statement: mda.org/press-releases/senat…
ALT The U.S. Capitol with text urging advocates to visit MDA.org/Medicaid.